Nonviral delivery of chemically modified tRNA rescues nonsense mutations in cystic fibrosis

Science作者:Jingan Chen, Muye Zhou, Songtao Dong, Fanglin Gong, Rasangi Tennakoon, Breanna Y. Seto, Ziyan Rachel Chen, Zhichang Peter Zhou, Jingyi Pan, Yue Xu, Sijin Luozhong, Colette Maya Macarios, Santiago Tijaro-Bulla, Tanja Gonska, Jim Hu, Haissi Cui, Bowen Li2026年8月27日正文已收录本站
Science, Volume 393, Issue 6814, August 2026.